News

January 3, 2019January 4, 2019

Data Point to Promise of Stem Cell Therapies for CALD Patients, Bluebird Bio Reports

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Bluebird Bio presented recent data from clinical trials in which two of its lead investigational therapies for cerebral adrenoleukodystrophy (CALD) were tested — a gene therapy that uses patient-derived stem ... Read more

December 21, 2018January 9, 2019

NeuroVia Starts Phase 1/2 Trial to Evaluate NV1205 in Childhood Cerebral Adrenoleukodystrophy

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[Editor’s Note updating article: According to ALD Life, the PEDALS trial investigating NV1205 as a potential treatment for adrenoleukodystrophy has been placed on a temporary hold by NeuroVia. A reason for ... Read more

December 19, 2018December 19, 2018

Phase 2/3 Trial of MIN-102 as Potential Treatment for AMN Ready to Dose Patients, Minoryx Reports

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Minoryx Therapeutics has finished randomizing patients in its ongoing Phase 2/3 clinical trial testing MIN-102, an investigational oral therapy for adrenomyeloneuropathy (AMN) – the most common type of X-linked adrenoleukodystrophy (X-ALD). A total ... Read more